Alglucosidase Alfa
Glycogen Storage Disease Due To Acid Maltase Deficiency, Late-Onset
Erasmus Medical Centerprotein_peptidePhase 4 / ApprovedActive
BBB
78/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 70/ 100
- Competitive Position
- 89/ 100
Competitive context
11 Active assets in the Glycogen Storage Disease Due To Acid Maltase Deficiency, Late-Onset cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
Cipaglucosidase Alfa Amicus Therapeutics | Phase 3 | BB |
Avalglucosidase Alfa Iris Plug | Phase 4 | BB |
at2221 Amicus Therapeutics | Phase 3 | B |
Miglustat Amicus Therapeutics | Phase 3 | B |
Clenbuterol Duke University | Phase 2 | CCC |
View all 13 →
Same molecule, other indications
Alglucosidase Alfa is also rated in:
glycogen storage disease due to acid maltase deficiency, infantile onsetDormant
BB
Indicative · Phase 4
69 / 100
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