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ARG

Neuromuscular Disease Caused By Qualitative Or Quantitative Defects Of Dystrophin

Massachusetts General HospitalSmall moleculePhase 1Dormant
CC
47/ 100
Provisional rating · Methodology v0.2

Rating breakdown

Clinical Evidence
32/ 100
Competitive Position
95/ 100

Competitive context

1 Active assets in the Neuromuscular Disease Caused By Qualitative Or Quantitative Defects Of Dystrophin cohort.

Same molecule, other indications

ARG is also rated in:

limb ischemiaDormant
BB
Indicative · Phase 4
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mitochondrial diseaseDormant
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69 / 100
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