Floatz logo

gc101

Spinal Muscular Atrophy

GeneCradle Incgene_therapyPhase 1/2Active
CC
47/ 100
Provisional rating · Methodology v0.2

Rating breakdown

Clinical Evidence
33/ 100
Competitive Position
89/ 100

Competitive context

19 Active assets in the Spinal Muscular Atrophy cohort.

Asset / SponsorPhaseRating
Nusinersen
Scholar Rock, Inc.
Phase 4A
Risdiplam
Scholar Rock, Inc.
Phase 4A
Non-Replicating Recombinant Self-Complementary (Sc) Adeno-Associated Virus Serotype 9 (Aav9) Vector Containing The Cdna Of The Survival Of Motor Neuron 2 (Smn2) Gene Under The Control Of The Hybrid Cytomegalovirus (Cmv) Enhancer/Chicken Beta-Actin Promoter (Cba)
Novartis Pharmaceuticals
Phase 4BBB
oav101
Novartis Pharmaceuticals
Phase 4BBB
Apitegromab
Scholar Rock, Inc.
Phase 3BB

View all 38 →

Same molecule, other indications

gc101 is also rated in:

melanomaActive
CCC
Indicative · Phase 2
55 / 100
View asset →
spinal muscular atrophy, type IIActive
CCC
Indicative · Phase 1/2
48 / 100
View asset →
spinal muscular atrophy, type IIIActive
CC
Indicative · Phase 1/2
47 / 100
View asset →

Need depth?

Order a full diligence report on this asset.

Order report →

Are you the sponsor?

Submit your data room for a Verified Rating. The public-data rating remains visible alongside.

Contact →