HUMAN IMMUNOGLOBULINS
Mucopolysaccharidosis
Takedaother_biologicalPhase 4 / ApprovedActive
B
62/ 100
Provisional rating · Methodology v0.2
Rating breakdown
- Clinical Evidence
- 47/ 100
- Competitive Position
- 95/ 100
Competitive context
5 Active assets in the Mucopolysaccharidosis cohort.
| Asset / Sponsor | Phase | Rating |
|---|---|---|
.BETA.-GLUCURONIDASE (SYNTHETIC HUMAN), HOMOTETRAMER Ultragenyx Pharmaceutical Inc | Phase 3 | BBB |
Rituximab Takeda | Phase 4 | BB |
Idursulfase Takeda | Phase 4 | BB |
METHOTREXATE Takeda | Phase 4 | BB |
Cyclophosphamide Masonic Cancer Center, University of Minnesota | Phase 2 | B |
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Same molecule, other indications
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