Floatz logo

Sat-3247

Duchenne Muscular Dystrophy

Explore 56 assets in Duchenne Muscular Dystrophy
Floatz Rating
B58/100
Confidence
Indicative
v0.2
Sponsor
Satellos Bioscience, Inc.
Modality
UNKNOWN
Development Phase
Phase 2
Status
Active
Evidence ledger · v0.2

Clinical Evidence

Clinical track record: trial progression, reported outcomes, safety signals, and endpoint quality.
45Moderate confidence
Detailed axis rationale is planned and will be published soon.
TrialPhaseStatusNPrimary endpointReadout
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
Recruiting
An Open-label Long-term Follow-up Study of SAT-3247 for Participants With Duchenne Muscular Dystrophy Including Those Who Participated in SAT-3247-CL-101
Enrolling By Invitation
First in Human SAD/MAD Safety and PK Study With Adult DMD Safety and PK Cohort
Completed

Competitive Position

Competitive setting: how crowded the indication is, class-level failures, and timing against rivals.
81High confidence
Detailed axis rationale is planned and will be published soon.

Same indication · Duchenne Muscular Dystrophy

AssetSponsorPhaseRating
Sat-3247 (this asset)Satellos Bioscience, Inc.P2B · 58
ViltolarsenNS Pharma, Inc.P4BBB
Aoc 1044Avidity Biosciences, Inc.P3BB
Delandistrogene MoxeparvovecSarepta Therapeutics, Inc.P3BB
GolodirsenRare Disease Research, LLCP4BB
PrednisoloneAnne M. ConnollyP4BB
EteplirsenSarepta Therapeutics, Inc.P3BB
GlutamineAssistance Publique - Hôpitaux de ParisP3BB
CasimersenKevin FlaniganP3BB

+41 more in the Duchenne Muscular Dystrophy cohort

Other indications for Sat-3247

IndicationSponsorPhaseRating
Neuromuscular DiseaseP2CCC · 53
Muscular DystrophyP2CCC · 53

Scientific Foundation

Strength of the underlying biology: target validation, tractability, modality fit, and how related mechanisms have fared.
NR

Planned for methodology v0.2.

Development Feasibility

How realistically the program can be executed, drawing on modality precedent, enrollment dynamics, and sponsor delivery.
NR

Planned for methodology v0.2.

Commercial Opportunity

Commercial prize: addressable population, unmet need, and the value case for the indication.
NR

Planned for methodology v0.2.

IP & Exclusivity

Exclusivity position, covering patent protection and freedom-to-operate runway.
NR

Planned for methodology v0.2.

Manufacturing & Supply

Manufacturing and supply readiness, driven by modality process and scale-up risk.
NR

Planned for methodology v0.2.

Related assets

Citation

Floatz Terminal. Sat-3247 in Duchenne Muscular Dystrophy. Methodology v0.2.
Rated under v0.2 effective July 8, 2026. Last refreshed July 8, 2026.
Accessed July 14, 2026.
https://terminal.floatz.ai/assets/sat-3247-duchenne-muscular-dystrophy

Need depth?

Order a full diligence report on this asset.

Order report →

Are you the sponsor?

Submit your data room for a Verified Rating. The public-data rating remains visible alongside.

Contact →