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Floatz Rating
B62/100
Confidence
Indicative
v0.2
Sponsor
Solid Biosciences Inc.
Modality
gene_therapy
Development Phase
Phase 3
Status
Active
Evidence ledger · v0.2

Clinical Evidence

Clinical track record: trial progression, reported outcomes, safety signals, and endpoint quality.
52Moderate confidence
Detailed axis rationale is planned and will be published soon.
TrialPhaseStatusNPrimary endpointReadout
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
Recruiting
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Recruiting

Competitive Position

Competitive setting: how crowded the indication is, class-level failures, and timing against rivals.
81High confidence
Detailed axis rationale is planned and will be published soon.

Same indication · Duchenne Muscular Dystrophy

AssetSponsorPhaseRating
Sgt-003 (this asset)Solid Biosciences Inc.P3B · 62
ViltolarsenNS Pharma, Inc.P4BBB
Aoc 1044Avidity Biosciences, Inc.P3BB
Delandistrogene MoxeparvovecSarepta Therapeutics, Inc.P3BB
GolodirsenRare Disease Research, LLCP4BB
PrednisoloneAnne M. ConnollyP4BB
GlutamineAssistance Publique - Hôpitaux de ParisP3BB
EteplirsenSarepta Therapeutics, Inc.P3BB
VamoroloneSanthera PharmaceuticalsP4BB

+41 more in the Duchenne Muscular Dystrophy cohort

Scientific Foundation

Strength of the underlying biology: target validation, tractability, modality fit, and how related mechanisms have fared.
NR

Planned for methodology v0.2.

Development Feasibility

How realistically the program can be executed, drawing on modality precedent, enrollment dynamics, and sponsor delivery.
NR

Planned for methodology v0.2.

Commercial Opportunity

Commercial prize: addressable population, unmet need, and the value case for the indication.
NR

Planned for methodology v0.2.

IP & Exclusivity

Exclusivity position, covering patent protection and freedom-to-operate runway.
NR

Planned for methodology v0.2.

Manufacturing & Supply

Manufacturing and supply readiness, driven by modality process and scale-up risk.
NR

Planned for methodology v0.2.

Related assets

Citation

Floatz Terminal. Sgt-003 in Duchenne Muscular Dystrophy. Methodology v0.2.
Rated under v0.2 effective July 8, 2026. Last refreshed July 8, 2026.
Accessed July 14, 2026.
https://terminal.floatz.ai/assets/sgt-003-duchenne-muscular-dystrophy

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