1 asset in GM1 Gangliosidosis Type 2
Therapeutic assets addressing GM1 Gangliosidosis Type 2, rated under Floatz methodology v0.2 and sorted by current rating.
| Asset | Sponsor | Phase | Rating |
|---|---|---|---|
Pbgm01 GM1 Gangliosidosis Type 2 | Gemma Biotherapeutics | P1/2 | NR () |