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62 assets in Hemophilia A

Therapeutic assets addressing Hemophilia A, rated under Floatz methodology v0.2 and sorted by current rating.

AssetSponsorPhaseRating
Turoctocog Alfa
Hemophilia A
Novo Nordisk A/SP4A (85)
Eptacog Alfa (Activated)
Hemophilia A
AryoGen Pharmed Co.P4A (84)
Rurioctocog Alfa Pegol
Hemophilia A
TakedaP4BBB (79)
bay94-9027
Hemophilia A
BayerP4BBB (78)
Immunoglobulin G4 [230-Proline,De-449-Lysine], Anti-(Human Blood-Coagulation Factor Ix)(Human Clone 0365-0001-9985 ?4-Chain), Disulfide With Human Clone 0365-0001-9985 ?-Chain, (228?226?),(231?229?)-Bis(Disulfide) With Anti-(Human Blood-Coagulation Factor X) Immunoglobulin G4 [228-Proline,405-Leucine,409-Lysine,De-447-Lysine] (Human Clone 0365-0001-8174 ?4-Chain) Disulfide With Human Clone 0365-0001-8174 ?-Chain
Hemophilia A
Novo Nordisk A/SP3BBB (78)
N8-GP
Hemophilia A
Novo Nordisk A/SP3BBB (78)
Emicizumab
Hemophilia A
Emory UniversityP4BBB (77)
Factor Viii (Human)
Hemophilia A
Hoffmann-La RocheP4BBB (76)
Fitusiran
Hemophilia A
SanofiP4BBB (76)
Advate
Hemophilia A
Runhui WUP4BBB (74)
Damoctocog Alfa Pegol
Hemophilia A
BayerP4BBB (74)
Coagulation Factor Viia
Hemophilia A
American Thrombosis and Hemostasis NetworkP4BBB (72)
Efanesoctocog Alfa
Hemophilia A
SanofiP4BBB (72)
Factor Ix
Hemophilia A
Tulane UniversityP4BBB (72)
Factor Viii Inhibitor Bypassing Fraction
Hemophilia A
Emory UniversityP4BBB (72)
Rfviia
Hemophilia A
Emory UniversityP4BBB (72)
Concizumab
Hemophilia A
Novo Nordisk A/SP3BB (68)
1-740-BLOOD COAGULATION FACTOR VIII (RECOMBINANT HUMAN SCT800 HEAVY CHAIN) FUSION PROTEIN WITH HUMAN BLOOD COAGULATION FACTOR VIII B DOMAIN FRAGMENT (14-AMINO ACID LINKER) FUSION PROTEIN WITH BLOOD COAGULATION FACTOR VIII (RECOMBINANT HUMAN SCT800 LIGHT CHAIN) (346-,718-,719-,723-,770-,786-O-SULFO-L-TYROSINE)
Hemophilia A
Sinocelltech Ltd.P4BB (67)
(1-743)-(1638-2332)-BLOOD-COAGULATION FACTOR VIII (SYNTHETIC HUMAN) FUSION PROTEIN WITH IMMUNOGLOBULIN G1 (SYNTHETIC HUMAN FC DOMAIN FRAGMENT), (1444-6'),(1447-9')-BIS(DISULFIDE) WITH IMMUNOGLOBULIN G1 (SYNTHETIC HUMAN FC DOMAIN FRAGMENT)
Hemophilia A
Margaret RagniP4BB (66)
Desmopressin
Hemophilia A
Groupe Maladies hémorragiques de BretagneP4BB (66)
Daratumumab
Hemophilia A
Institute of Hematology & Blood Diseases Hospital, ChinaP4BB (64)
Antihemophilic Factor,Human,Method M,Monoclonal
Hemophilia A
Dhaka Medical CollegeP3B (62)
Ehl-Fviii
Hemophilia A
Federico II UniversityP4B (62)
Valoctocogene Roxaparvovec
Hemophilia A
BioMarin PharmaceuticalP3B (62)
Antihemophilic Factor, Human Recombinant Residues 722-1672 Deleted
Hemophilia A
OctapharmaP4B (60)
kn057
Hemophilia A
Suzhou Alphamab Co., Ltd.P3B (60)
Antithrombin Iii
Hemophilia A
SanofiP4B (59)
Dirloctocogene Samoparvovec
Hemophilia A
Spark Therapeutics, Inc.P3B (59)
Dpc-A69448
Hemophilia A
Hangzhou Gensciences Biopharmaceutical Co., Ltd.P1/2B (59)
nxt007
Hemophilia A
Hoffmann-La RocheP3B (59)
Immunoglobulin G1, Anti-(Human Tissue Factor Pathway Inhibitor) (Human Monoclonal Pf-06741086 .Gamma.1-Chain), Disulfide With Human Monoclonal Pf-06741086 .Lambda.-Chain, Dimer
Hemophilia A
PfizerP3B (57)
Wilate
Hemophilia A
Emory UniversityP4B (56)
Emicizumab-Kxwh
Hemophilia A
Montefiore Medical CenterP3CCC (54)
Giroctocogene Fitelparvovec Transgene Insert
Hemophilia A
PfizerP3CCC (54)
gs1191-0445
Hemophilia A
Gritgen Therapeutics Co., Ltd.P3CCC (54)
Recombinant Human Activated Coagulation Factor Vii For
Hemophilia A
Chia Tai Tianqing Pharmaceutical Group Co., Ltd.P3CCC (54)
Recombinant Human Activated Coagulation Factor Viii For
Hemophilia A
Chia Tai Tianqing Pharmaceutical Group Nanjing Shunxin Pharmaceutical Co., Ltd.P3CCC (54)
Spk-8016
Hemophilia A
Spark Therapeutics, Inc.P1/2CCC (52)
nnc0442-0344 a
Hemophilia A
Novo Nordisk A/SP1CCC (50)
Serpinpc
Hemophilia A
ApcinteX LtdP3CCC (48)
sr604
Hemophilia A
Shanghai RAAS Blood Products Co., Ltd.P1/2CCC (48)
AAV-2
Hemophilia A
University College, LondonP1/2CC (43)
aav2/8-hlp-fviii-v3
Hemophilia A
University College, LondonP1/2CC (43)
Anb-010, Dose 1
Hemophilia A
BiocadP1/2CC (43)
Anb-010, Dose 3
Hemophilia A
BiocadP1/2CC (43)
asc618
Hemophilia A
ASC TherapeuticsP1/2CC (43)
bay2599023
Hemophilia A
BayerP1/2CC (43)
Spk-8011Qq
Hemophilia A
Hoffmann-La RocheP1/2CC (43)
Auto-Cd34+ Cells
Hemophilia A
Christian Medical College, Vellore, IndiaP1CC (42)
Auto Cd34+Pbsc Transduced With A Lentiviral Vector Encoding A Novel Coagulation Factor Viii Transgene
Hemophilia A
Christian Medical College, Vellore, IndiaP1CC (42)
Showing 1 to 50 of 62 assets
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