1 asset in Leber Congenital Amaurosis 10
Therapeutic assets addressing Leber Congenital Amaurosis 10, rated under Floatz methodology v0.2 and sorted by current rating.
| Asset | Sponsor | Phase | Rating |
|---|---|---|---|
Sepofarsen Leber Congenital Amaurosis 10 | Laboratoires Thea | P3 | NR () |