Floatz logo

22 assets in Mucopolysaccharidosis Type 2

Therapeutic assets addressing Mucopolysaccharidosis Type 2, rated under Floatz methodology v0.2 and sorted by current rating.

AssetSponsorPhaseRating
Idursulfase
Mucopolysaccharidosis Type 2
TakedaP4A (86)
Pabinafusp Alfa
Mucopolysaccharidosis Type 2
JCR Pharmaceuticals Co., Ltd.P3BBB (78)
Rgx-121
Mucopolysaccharidosis Type 2
REGENXBIO Inc.P3BB (70)
Rituximab
Mucopolysaccharidosis Type 2
TakedaP4BB (68)
Gnr-055
Mucopolysaccharidosis Type 2
AO GENERIUMP2/3BB (64)
Tividenofusp Alfa
Mucopolysaccharidosis Type 2
Denali Therapeutics Inc.P2/3BB (64)
Human Immunoglobulins
Mucopolysaccharidosis Type 2
TakedaP4B (62)
Methotrexate
Mucopolysaccharidosis Type 2
TakedaP4B (60)
Busulfanum
Mucopolysaccharidosis Type 2
Masonic Cancer Center, University of MinnesotaP2B (57)
Cald Hr-D
Mucopolysaccharidosis Type 2
Masonic Cancer Center, University of MinnesotaP2CCC (53)
Adalimumab
Mucopolysaccharidosis Type 2
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical CenterP1/2CCC (52)
Apoeii
Mucopolysaccharidosis Type 2
University of ManchesterP1/2CCC (48)
Autologous Cd34+ Cells Transduced With Tns9.3.55
Mucopolysaccharidosis Type 2
University of ManchesterP1/2CCC (48)
Autologous Cd34+ Hscs Transduced Ex Vivo With Cd11B Lv Encoding Human Ids Tagged With Apoeii
Mucopolysaccharidosis Type 2
University of ManchesterP1/2CCC (48)
sb-913
Mucopolysaccharidosis Type 2
Sangamo TherapeuticsP1/2CCC (48)
Verenafusp Alfa
Mucopolysaccharidosis Type 2
AO GENERIUMP1CC (47)
Duoc-01
Mucopolysaccharidosis Type 2
Joanne Kurtzberg, MDP1CC (43)
gc1123
Mucopolysaccharidosis Type 2
GC Biopharma CorpP1CC (43)
Genetic Hmi-203
Mucopolysaccharidosis Type 2
Homology Medicines, IncP1CC (43)
Iduronidase, .Alpha.-L-(8-Histidine) (Human)
Mucopolysaccharidosis Type 2
University of California, San FranciscoP1CC (43)