Floatz logo

11 assets in Wilson Disease

Therapeutic assets addressing Wilson Disease, rated under Floatz methodology v0.2 and sorted by current rating.

AssetSponsorPhaseRating
Teta 4Hcl
Wilson Disease
OrphalanP3BBB (73)
Zinc D-Gluconate (1:2)
Wilson Disease
Jun LiP4BBB (72)
Penicillamine
Wilson Disease
OrphalanP3BB (69)
Alxn1840
Wilson Disease
Alexion Pharmaceuticals, Inc.P3BB (66)
Gandouling
Wilson Disease
Jun LiP4BB (65)
Ly-M003
Wilson Disease
Lingyi Biotech Co., Ltd.P1/2CCC (54)
Capsomere, Recombinant Human Adeno-Associated Virus Aav3B Viral Capsid Protein Vp1-Vp2-Vp3 Complex (1:2:7), Hexacontamer, Complex With Dna (Recombinant Replication-Defective Adeno-Associated Virus Serotype 3B Vector Vtx-801 Liver-Specific Human ?-1 Antitrypsin Promoter Plus Human 57-486-Copper Transporter Atp7B Codon-Optimized Gene Plus Rabbit ?-Globin Polyadenylation Signal Plus Adeno-Associated Virus 2 Inverted Terminal Repeat Flanks) (1:1)
Wilson Disease
Vivet Therapeutics SASP1/2CCC (48)
Dna (Recombinant Replication-Defective Adeno-Associated Virus Serotype 9 Vector Ux701 Murine Transthyretin Enhancer Plus Human Transthyretin Promoter Plus Simian Virus 40 Intron Plus Human Adenosine Triphosphatase Copper-Transporting ? Metal-Binding Domain 4/5/6 Transgene Atp7B-Mbd456 Plus Simian Virus 40 Polyadenylation Signal Plus Adeno-Associated Virus 2 Inverted Terminal Repeat Flanks Plus Adeno-Associated Virus 2 Rep Region Plus Adeno-Associated Virus 9 Cap Region-Specifying)
Wilson Disease
Ultragenyx Pharmaceutical IncP1/2CC (47)
DSL101
Wilson Disease
DSciLab Co., Ltd.Early P1C (39)
gc310
Wilson Disease
GeneCradle IncP1/2NR ()
Mwav201
Wilson Disease
Xinhua Hospital, Shanghai Jiao Tong University School of MedicineN/ANR ()