Floatz logo

(6S)-L-ERYTHRO-TETRAHYDROBIOPTERIN

Hyperphenylalaninemia Due To Tetrahydrobiopterin Deficiency

Floatz Rating
CC43/100
Confidence
Indicative
v0.2
Sponsor
University of Massachusetts, Amherst
Modality
Small molecule
Development Phase
Phase 1
Status
Dormant
Evidence ledger · v0.2

Clinical Evidence

Clinical track record: trial progression, reported outcomes, safety signals, and endpoint quality.
28High confidence
Detailed axis rationale is planned and will be published soon.
TrialPhaseStatusNPrimary endpointReadout
O2 Transport and Utilization in Health and Lung Disease
Withdrawn
Bone Mineral Density in Adults With Hyperphenylalaninemia on Kuvan Therapy
Terminated

Competitive Position

Competitive setting: how crowded the indication is, class-level failures, and timing against rivals.
95High confidence
Detailed axis rationale is planned and will be published soon.

Same indication · Hyperphenylalaninemia Due To Tetrahydrobiopterin Deficiency

AssetSponsorPhaseRating
(6S)-L-ERYTHRO-TETRAHYDROBIOPTERIN (this asset)University of Massachusetts, AmherstP1CC · 43
SepiapterinPTC TherapeuticsP1/2CCC
PhenoptinBioMarin PharmaceuticalP2NR
Sapropterin DihydrochlorideBioMarin PharmaceuticalUnkNR

Other indications for (6S)-L-ERYTHRO-TETRAHYDROBIOPTERIN

IndicationSponsorPhaseRating
Lesch-Nyhan SyndromeP2/3B · 56
Portal HypertensionP2/3B · 56
PhenylketonuriaP2CCC · 53

Scientific Foundation

Strength of the underlying biology: target validation, tractability, modality fit, and how related mechanisms have fared.
NR

Planned for methodology v0.2.

Development Feasibility

How realistically the program can be executed, drawing on modality precedent, enrollment dynamics, and sponsor delivery.
NR

Planned for methodology v0.2.

Commercial Opportunity

Commercial prize: addressable population, unmet need, and the value case for the indication.
NR

Planned for methodology v0.2.

IP & Exclusivity

Exclusivity position, covering patent protection and freedom-to-operate runway.
NR

Planned for methodology v0.2.

Manufacturing & Supply

Manufacturing and supply readiness, driven by modality process and scale-up risk.
NR

Planned for methodology v0.2.

Related assets

Citation

Floatz Terminal. (6S)-L-ERYTHRO-TETRAHYDROBIOPTERIN in Hyperphenylalaninemia Due To Tetrahydrobiopterin Deficiency. Methodology v0.2.
Rated under v0.2 effective July 8, 2026. Last refreshed July 8, 2026.
Accessed July 14, 2026.
https://terminal.floatz.ai/assets/6s-l-erythro-tetrahydrobiopterin-hyperphenylalaninemia-due-to-tetrahydrobiopterin-deficiency

Need depth?

Order a full diligence report on this asset.

Order report →

Are you the sponsor?

Submit your data room for a Verified Rating. The public-data rating remains visible alongside.

Contact →